Search for Clinical Trial Results
Leukodystrophy - 153 Studies Found
Status | Study |
Completed |
Study Name: The Natural History of Infantile Globoid Cell Leukodystrophy Condition: Infantile Globoid Cell Leukodystrophy Date: 2009-09-23 |
Completed |
Study Name: Long-term Metazym Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) Condition: Late Infantile Metachromatic Leukodystrophy Date: 2008-02-29 Interventions: Biological: Recombinant human Arylsulfatase A (rhASA) intravenous infusion, every other week for 26 week |
Completed |
Study Name: Imaging Study of the White Matter Lesions in Children With Metachromatic Leucodystrophy Condition: Late Infantile Metachromatic Leukodystrophy Date: 2011-03-09 Interventions: Other: High-field MRI (3 Teslas) |
Enrolling by invitation |
Study Name: Open-Label Extension Study Evaluating Safety and Efficacy of HGT-1110 in Patients With Metachromatic Leukodystrophy Condition: Metachromatic Leukodystrophy (MLD) Date: 2013-06-20 Interventions:
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Completed |
Study Name: Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) Condition: Metachromatic Leukodystrophy (MLD) Date: 2007-01-04 Interventions: Drug: rhASA intravenous infusion 25 U/kg,50 U/kg, 100U/kg or 200 U/kg every other week for 26 weeks |
Recruiting |
Study Name: Natural History of the Leukodystrophies Condition: Leukodystrophies Date: 2016-04-07 |
Completed |
Study Name: Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation Condition: Metachromatic Leukodystrophy Date: 2011-02-23 Interventions: Drug: rhARSA intravenous infusion 100U/kg every other week for 18 months |
Terminated |
Study Name: Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD Condition: Late Infantile Metachromatic Leukodystrophy Date: 2008-05-19 Interventions: Drug: HGT-1111 Patients currently dosed with 100 U/kg or 200 U/kg will continue this treatment. Patients |
Recruiting |
Study Name: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy Condition:
Date: 2015-08-12 Interventions: Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
Recruiting |
Study Name: The Nosology and Etiology of Leukodystrophies of Unknown Causes Condition:
Date: 2009-04-25 |